TY - JOUR T1 - Enzyme replacement therapy for mucopolysaccharidosis VI: Long-term cardiac effects of galsulfase (Naglazyme®) therapy JF - Journal of Inherited Metabolic Disease Y1 - 2013 A1 - Braunlin, E. A1 - Rosenfeld, H. A1 - Kampmann, C. A1 - Johnson, J. A1 - Beck, M. A1 - Giugliani, R. A1 - Guffon, N. A1 - Ketteridge, D. A1 - SáMiranda, C. M. A1 - Scarpa, M. A1 - Schwartz, I. V. A1 - Leão Teles, E. A1 - Wraith, J.E. A1 - Barrios, P. A1 - Dias da Silva, E. A1 - Kurio, G. A1 - Richardson, M. A1 - Gildengorin, G. A1 - Hopwood, J.J. A1 - Imperiale, M. A1 - Schatz, A. A1 - Decker, C. A1 - Harmatz, P. VL - 36 UR - http://www.scopus.com/inward/record.url?eid=2-s2.0-84879684477&partnerID=40&md5=809f269d1e1f742fd6dc536bbf98b56b IS - 2 N1 - Cited By (since 1996):6Export Date: 8 April 2014Source: Scopus ER - TY - ABST T1 - Enzyme replacement therapy for mucopolysaccharidosis VI: long-term cardiac effects of galsulfase (Naglazyme ®) therapy Y1 - 2012 A1 - Braunlin, E. A1 - Rosenfeld, H. A1 - Kampmann, C. A1 - Johnson, J. A1 - Beck, M. A1 - Giugliani, R. A1 - Guffon, N. A1 - Ketteridge, D. A1 - SáMiranda, C. M. A1 - Scarpa, M. A1 - Schwartz, I. V. A1 - Leão Teles, E. A1 - Wraith, J.E. A1 - Barrios, P. A1 - Dias da Silva, E. A1 - Kurio, G. A1 - Richardson, M. A1 - Gildengorin, G. A1 - Hopwood, J.J. A1 - Imperiale, M. A1 - Schatz, A. A1 - Decker, C. A1 - Harmatz, P. JF - Journal of Inherited Metabolic Disease UR - http://www.scopus.com/inward/record.url?eid=2-s2.0-84861722683&partnerID=40&md5=cada11c663bff78563ca271d528303bb N1 - Export Date: 18 March 2013Source: ScopusArticle in Press ER - TY - JOUR T1 - Enzyme replacement therapy for mucopolysaccharidosis VI: Evaluation of long-term pulmonary function in patients treated with recombinant human N-acetylgalactosamine 4-sulfatase JF - Journal of Inherited Metabolic Disease Y1 - 2010 A1 - Harmatz, P. A1 - Yu, Z.-F. A1 - Giugliani, R. A1 - Schwartz, I.V.D. A1 - Guffon, N. A1 - Teles, E.L. A1 - Miranda, M.C.S. A1 - Wraith, J.E. A1 - Beck, M. A1 - Arash, L. A1 - Scarpa, M. A1 - Ketteridge, D. A1 - Hopwood, J.J. A1 - Plecko, B. A1 - Steiner, R. A1 - Whitley, C.B. A1 - Kaplan, P. A1 - Swiedler, S.J. A1 - Hardy, K. A1 - Berger, K.I. A1 - Decker, C. VL - 33 UR - http://www.scopus.com/inward/record.url?eid=2-s2.0-77649237484&partnerID=40&md5=b0a62e125234c3e1d9c52bde100b1f47 IS - 1 N1 - Cited By (since 1996): 13Export Date: 18 March 2013Source: Scopus ER - TY - JOUR T1 - Enzyme replacement therapy for mucopolysaccharidosis VI: Growth and pubertal development in patients treated with recombinant human N-acetylgalactosamine 4-sulfatase JF - Journal of Pediatric Rehabilitation Medicine Y1 - 2010 A1 - Decker, C. A1 - Yu, Z.-F. A1 - Giugliani, R. A1 - Schwartz, I.V.D. A1 - Guffon, N. A1 - Teles, E.L. A1 - Miranda, M.C.S. A1 - Wraith, J.E. A1 - Beck, M. A1 - Arash, L. A1 - Scarpa, M. A1 - Ketteridge, D. A1 - Hopwood, J.J. A1 - Plecko, B. A1 - Steiner, R. A1 - Whitley, C.B. A1 - Kaplan, P. A1 - Swiedler, S.J. A1 - Conrad, S. A1 - Harmatz, P. VL - 3 UR - http://www.scopus.com/inward/record.url?eid=2-s2.0-77954629021&partnerID=40&md5=9d8b9a8582dbf72c9ab58a33205e09a7 IS - 2 N1 - Cited By (since 1996): 11Export Date: 18 March 2013Source: Scopus ER - TY - JOUR T1 - Long-term follow-up of endurance and safety outcomes during enzyme replacement therapy for mucopolysaccharidosis VI: Final results of three clinical studies of recombinant human N-acetylgalactosamine 4-sulfatase JF - Molecular Genetics and Metabolism Y1 - 2008 A1 - Harmatz, P. A1 - Giugliani, R. A1 - D. Schwartz, I.V. A1 - Guffon, N. A1 - Teles, E.L. A1 - Miranda, M.C.S. A1 - Wraith, J.E. A1 - Beck, M. A1 - Arash, L. A1 - Scarpa, M. A1 - Ketteridge, D. A1 - Hopwood, J.J. A1 - Plecko, B. A1 - Steiner, R. A1 - Whitley, C.B. A1 - Kaplan, P. A1 - Yu, Z.-F. A1 - Swiedler, S.J. A1 - Decker, C. VL - 94 UR - http://www.scopus.com/inward/record.url?eid=2-s2.0-46949093352&partnerID=40&md5=3cf7db34b2fa5e51f33003e05d528b75 IS - 4 N1 - Cited By (since 1996): 60Export Date: 18 March 2013Source: Scopus ER -