TY - JOUR T1 - Enzyme replacement therapy for mucopolysaccharidosis VI: Evaluation of long-term pulmonary function in patients treated with recombinant human N-acetylgalactosamine 4-sulfatase JF - Journal of Inherited Metabolic Disease Y1 - 2010 A1 - Harmatz, P. A1 - Yu, Z.-F. A1 - Giugliani, R. A1 - Schwartz, I.V.D. A1 - Guffon, N. A1 - Teles, E.L. A1 - Miranda, M.C.S. A1 - Wraith, J.E. A1 - Beck, M. A1 - Arash, L. A1 - Scarpa, M. A1 - Ketteridge, D. A1 - Hopwood, J.J. A1 - Plecko, B. A1 - Steiner, R. A1 - Whitley, C.B. A1 - Kaplan, P. A1 - Swiedler, S.J. A1 - Hardy, K. A1 - Berger, K.I. A1 - Decker, C. VL - 33 UR - http://www.scopus.com/inward/record.url?eid=2-s2.0-77649237484&partnerID=40&md5=b0a62e125234c3e1d9c52bde100b1f47 IS - 1 N1 - Cited By (since 1996): 13Export Date: 18 March 2013Source: Scopus ER - TY - JOUR T1 - Enzyme replacement therapy for mucopolysaccharidosis VI: Growth and pubertal development in patients treated with recombinant human N-acetylgalactosamine 4-sulfatase JF - Journal of Pediatric Rehabilitation Medicine Y1 - 2010 A1 - Decker, C. A1 - Yu, Z.-F. A1 - Giugliani, R. A1 - Schwartz, I.V.D. A1 - Guffon, N. A1 - Teles, E.L. A1 - Miranda, M.C.S. A1 - Wraith, J.E. A1 - Beck, M. A1 - Arash, L. A1 - Scarpa, M. A1 - Ketteridge, D. A1 - Hopwood, J.J. A1 - Plecko, B. A1 - Steiner, R. A1 - Whitley, C.B. A1 - Kaplan, P. A1 - Swiedler, S.J. A1 - Conrad, S. A1 - Harmatz, P. VL - 3 UR - http://www.scopus.com/inward/record.url?eid=2-s2.0-77954629021&partnerID=40&md5=9d8b9a8582dbf72c9ab58a33205e09a7 IS - 2 N1 - Cited By (since 1996): 11Export Date: 18 March 2013Source: Scopus ER - TY - JOUR T1 - Long-term follow-up of endurance and safety outcomes during enzyme replacement therapy for mucopolysaccharidosis VI: Final results of three clinical studies of recombinant human N-acetylgalactosamine 4-sulfatase JF - Molecular Genetics and Metabolism Y1 - 2008 A1 - Harmatz, P. A1 - Giugliani, R. A1 - D. Schwartz, I.V. A1 - Guffon, N. A1 - Teles, E.L. A1 - Miranda, M.C.S. A1 - Wraith, J.E. A1 - Beck, M. A1 - Arash, L. A1 - Scarpa, M. A1 - Ketteridge, D. A1 - Hopwood, J.J. A1 - Plecko, B. A1 - Steiner, R. A1 - Whitley, C.B. A1 - Kaplan, P. A1 - Yu, Z.-F. A1 - Swiedler, S.J. A1 - Decker, C. 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VL - 28 UR - http://www.scopus.com/inward/record.url?eid=2-s2.0-34547673433&partnerID=40&md5=a23ac7304a5def19685c11fa229c1879 IS - 9 N1 - Cited By (since 1996): 31Export Date: 18 March 2013Source: Scopus ER - TY - JOUR T1 - Enzyme replacement therapy for mucopolysaccharidosis VI: A phase 3, randomized, double-blind, placebo-controlled, multinational study of recombinant human N-acetylgalactosamine 4-sulfatase (recombinant human arylsulfatase B or rhASB) and follow-on, open-l JF - Journal of Pediatrics Y1 - 2006 A1 - Harmatz, P. A1 - Giugliani, R. A1 - Schwartz, I. A1 - Guffon, N. A1 - Teles, E.L. A1 - Miranda, M.C.S. A1 - Wraith, J.E. A1 - Beck, M. A1 - Arash, L. A1 - Scarpa, M. A1 - Yu, Z.-F. A1 - Wittes, J. A1 - Berger, K.I. A1 - Newman, M.S. A1 - Lowe, A.M. A1 - Kakkis, E. A1 - Swiedler, S.J. VL - 148 UR - http://www.scopus.com/inward/record.url?eid=2-s2.0-33744978567&partnerID=40&md5=0620094eea7917a76536626611bb8a8c IS - 4 N1 - Cited By (since 1996): 148Export Date: 18 March 2013Source: Scopus ER - TY - JOUR T1 - Direct comparison of measures of endurance, mobility, and joint function during enzyme-replacement therapy of mucopolysaccharidosis VI (Maroteaux-Lamy syndrome): Results after 48 weeks in a phase 2 open-label clinical study of recombinant human N-acetylga JF - Pediatrics Y1 - 2005 A1 - Harmatz, P. A1 - Ketteridge, D. A1 - Giugliani, R. A1 - Guffon, N. A1 - Teles, E.L. A1 - Miranda, M.C.S. A1 - Yu, Z.-F. A1 - Swiedler, S.J. A1 - Hopwood, J.J. VL - 115 UR - http://www.scopus.com/inward/record.url?eid=2-s2.0-27744493202&partnerID=40&md5=5cd4badc420144129a7b5092723f0d06 IS - 6 N1 - Cited By (since 1996): 90Export Date: 18 March 2013Source: Scopus ER - TY - JOUR T1 - Threshold effect of urinary glycosaminoglycans and the walk test as indicators of disease progression in a survey of subjects with Mucopolysaccharidosis VI (Maroteaux-Lamy syndrome) JF - American Journal of Medical Genetics Y1 - 2005 A1 - Swiedler, S.J. A1 - Beck, M. A1 - Bajbouj, M. A1 - Giugliani, R. A1 - Schwartz, I. A1 - Harmatz, P. A1 - Wraith, J.E. A1 - Roberts, J. A1 - Ketteridge, D. A1 - Hopwood, J.J. A1 - Guffon, N. A1 - Sá Miranda, M.C. A1 - Teles, E.L. A1 - Berger, K.I. A1 - Piscia-Nichols, C. VL - 134 A UR - http://www.scopus.com/inward/record.url?eid=2-s2.0-20144386995&partnerID=40&md5=9c8cfc3e51a0cff4dbcd8a9b70a70aad IS - 2 N1 - Cited By (since 1996): 41Export Date: 18 March 2013Source: Scopus ER -