TitleEnzyme replacement therapy for mucopolysaccharidosis VI: Long-term cardiac effects of galsulfase (Naglazyme®) therapy
Publication TypeJournal Article
Year of Publication2013
AuthorsBraunlin, E, Rosenfeld, H, Kampmann, C, Johnson, J, Beck, M, Giugliani, R, Guffon, N, Ketteridge, D, SáMiranda, CM, Scarpa, M, Schwartz, IV, Leão Teles, E, Wraith, JE, Barrios, P, Dias da Silva, E, Kurio, G, Richardson, M, Gildengorin, G, Hopwood, JJ, Imperiale, M, Schatz, A, Decker, C, Harmatz, P
JournalJournal of Inherited Metabolic Disease
Volume36
Issue2
Pagination385 - 394
Date Published2013
URLhttp://www.scopus.com/inward/record.url?eid=2-s2.0-84879684477&partnerID=40&md5=809f269d1e1f742fd6dc536bbf98b56b

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